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Adrian Krainer wins RNA Society’s Lifetime Achievement Award

March 8, 2019

Professor Adrian Krainer was awarded the RNA Society’s Lifetime Achievement Award for his life-saving research.

National Academy of Inventors Fellow, Adrian Krainer

December 11, 2018

Professor Adrian Krainer has been named a NAI 2018 Fellow for his work on the first FDA-approved treatment for spinal muscular atrophy.

Big bold dreamers

December 10, 2018

Dreamers drive discoveries. CSHL honors its many scientists making big impacts in their respective fields.

Breakthrough Prize laureates meet at CSHL

December 6, 2018

Breakthrough Prize winner Adrian Krainer & C. Frank Bennett reunite for the first time since their award ceremony at CSHL to discuss further project.

Breakthrough Prize to CSHL professor for SMA research

October 17, 2018

Professor Adrian Krainer has received a Breakthrough Prize in Life Sciences for his work on the first FDA-approved treatment of SMA.

CSHL helps ring opening bell at Nasdaq

August 21, 2018

CSHL Professor Adrian Krainer and his team join the Spinal Muscular Atrophy (SMA) Foundation in ringing the Nasdaq opening bell

FDA approval of life-saving SMA drug is hailed by its researcher-inventor at CSHL

December 24, 2016

Nusinersen (Spinraza) will be used to treat young children with a severe and potentially fatal illness called spinal muscular atrophy (SMA).

One experiment: A drug for SMA visibly repairs defective cells

December 1, 2016

Professor Adrian Krainer develops a treatment for spinal muscular atrophy, the leading genetic cause of infant death.

“Sink or swim”

October 15, 2016

This episode of Base Pairs follows Professor Adrian Krainer and his experience as the first CSHL fellow.

Candidate drug for spinal muscular atrophy, with roots in CSHL research, passes major hurdle

August 4, 2016

Biotechnology firms Biogen and Ionis Pharmaceuticals cut short a phase-3 clinical trial for the investigational drug nusinersen as it met endpoint.

Adrian Krainer of Cold Spring Harbor Laboratory elected to American Academy of Arts and Sciences

April 20, 2016

Adrian Krainer was elected to the American Academy of Arts and Sciences.

Mechanistic insights into spinal muscular atrophy suggest new paths for treatment

January 12, 2015

Researchers find that in mouse models of the disease subcutaneous drug administration is sufficient to treat SMA

First animal model of adult-onset SMA sheds light on disease progression and treatment

September 9, 2013

Another proof of principle for TSUNAMI method in modeling spinal muscular atrophy and other splicing-related illnesses

CSHL-led team introduces new method to closely model diseases caused by splicing defects

August 15, 2012

Researchers find novel method of making animal models for human genetic disease research.

Splicing studies detail a protein’s role in creating cancer’s mixed messages

February 13, 2012

Adrian Krainer discusses alternative splicing and how it can be used to treat diseases like cancer and spinal muscular atrophy.

CSHL Story archive for Tag: SMA