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CSHL Story Archive for Tag: SMA

FDA approval of life-saving SMA drug is hailed by its researcher-inventor at CSHL

FDA approval of life-saving SMA drug is hailed by its researcher-inventor at CSHL

December 24, 2016

One experiment: A drug for SMA visibly repairs defective cells

One experiment: A drug for SMA visibly repairs defective cells

December 1, 2016

“Sink or swim”

“Sink or swim”

October 15, 2016

Candidate drug for spinal muscular atrophy, with roots in CSHL research, passes major hurdle

Candidate drug for spinal muscular atrophy, with roots in CSHL research, passes major hurdle

August 4, 2016

Adrian Krainer of Cold Spring Harbor Laboratory elected to American Academy of Arts and Sciences

Adrian Krainer of Cold Spring Harbor Laboratory elected to American Academy of Arts and Sciences

April 20, 2016

Mechanistic insights into spinal muscular atrophy suggest new paths for treatment

Mechanistic insights into spinal muscular atrophy suggest new paths for treatment

January 12, 2015

First animal model of adult-onset SMA sheds light on disease progression and treatment

First animal model of adult-onset SMA sheds light on disease progression and treatment

September 9, 2013

CSHL-led team introduces new method to closely model diseases caused by splicing defects

CSHL-led team introduces new method to closely model diseases caused by splicing defects

August 15, 2012

Splicing studies detail a protein’s role in creating cancer’s mixed messages

Splicing studies detail a protein’s role in creating cancer’s mixed messages

February 13, 2012

Antisense therapy delivers long-term correction of severe Spinal Muscular Atrophy in mice

Antisense therapy delivers long-term correction of severe Spinal Muscular Atrophy in mice

October 5, 2011

Collaboration column: SMA therapeutics and potential drug target for schizophrenia

Collaboration column: SMA therapeutics and potential drug target for schizophrenia

March 11, 2011

CSHL researchers demonstrate efficacy of antisense therapy for spinal muscular atrophy

CSHL researchers demonstrate efficacy of antisense therapy for spinal muscular atrophy

July 12, 2010

Researchers identify drug candidate for treating spinal muscular atrophy

Researchers identify drug candidate for treating spinal muscular atrophy

November 4, 2009

Cold Spring Harbor Laboratory scientists devise potential approach to treat spinal muscular atrophy

Cold Spring Harbor Laboratory scientists devise potential approach to treat spinal muscular atrophy

April 4, 2008

CSHL shows correcting RNA splicing may help treat spinal muscular atrophy

CSHL shows correcting RNA splicing may help treat spinal muscular atrophy

March 12, 2007