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 yeah<00:00:00.240> I<00:00:00.320> mean<00:00:00.480> I<00:00:00.760> I<00:00:00.960> do<00:00:01.160> want<00:00:01.319> to<00:00:01.480> stress<00:00:01.880> how

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yeah I mean I I do want to stress how
 
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yeah I mean I I do want to stress how
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important it is to pursue the the basic
 
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important it is to pursue the the basic
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science understanding the fundamentals
 
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science understanding the fundamentals
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of a process like RNA splicing we
 
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of a process like RNA splicing we
realized<00:00:09.639> that<00:00:09.960> that<00:00:10.080> it's<00:00:10.320> relevant<00:00:10.679> for

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realized that that it's relevant for
 
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realized that that it's relevant for
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disease but we didn't necessarily think
 
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disease but we didn't necessarily think
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ah uh this is immediately going to lead
 
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ah uh this is immediately going to lead
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to a cure but but there's always the the
 
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to a cure but but there's always the the
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potential sometimes the illusion that
 
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potential sometimes the illusion that
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the more you understand the more you or
 
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the more you understand the more you or
somebody<00:00:24.119> else<00:00:24.359> may<00:00:24.599> come<00:00:24.800> up<00:00:25.400> with<00:00:25.519> a<00:00:25.760> therapy

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somebody else may come up with a therapy
 
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somebody else may come up with a therapy
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based on this knowledge that can then
 
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based on this knowledge that can then
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really improve the lives of of patient
 
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really improve the lives of of patient
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so that's always a a strong motivator
 
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so that's always a a strong motivator
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and certainly as I have met many SMA
 
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and certainly as I have met many SMA
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patients and their families that has
 
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patients and their families that has
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always been uh very inspiring along the
 
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always been uh very inspiring along the
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way to to press on and to to uh to work
 
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way to to press on and to to uh to work
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hard to try to solve this problem and
 
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hard to try to solve this problem and
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and so it isn't just abstract you know
 
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and so it isn't just abstract you know
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splicing but but that is of course very
 
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splicing but but that is of course very
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important but we do have in mind the
 
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important but we do have in mind the
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